Found 82 matching trials
Epidemiological Study of Fabry Disease in Taiwan Young Stroke Patients
N/AEpidemiological Study of Fabry Disease in Taiwan Young Stroke Patients...
Location
Multiple Locations
Open Label Extension Study of 1 mg/kg Pegunigalsidase Alfa Every 2 Weeks in Patients With Fabry Disease
PHASE3The objective of CLI-06657AA1-04 (formerly PB-102-F60) was to evaluate the ...
Natural History in Fabry Disease With IVS4+919G>A Mutations
N/AFabry disease (FD) is a genetic condition where mutations in the GLA gene c...
Status
Active Not Recruiting
Location
Division of Cardiology, Department of Medicine and Therapeutics Faculty of Medicine, The Chinese University of Hong Kong
Treatment Protocol of Replagal for Patients With Fabry Disease
N/AThe study will evaluate the safety and efficacy of Replagal® (agalsidase al...
Status
No Longer Available
Location
AKDHC Tucson Campbell
Efficacy and Safety of Enzyme Replacement Therapy in Patients With Fabry Disease
N/AThe goal of this observational study is to learn how enzyme replacement the...
Status
Enrolling By Invitation
Open Label Extension of 2 mg/kg Pegunigalsidase Alfa (PRX-102) Every 4 Weeks in Adult Fabry Disease Patients
PHASE3The objective of CLI-06657AA1-03 (formerly PB-102-F51) is to evaluate the l...
Home Therapy With Replagal in Fabry Disease
N/AThe purpose of this study is to proof increasing patient satisfaction and p...
Location
Landeskrankenhaus Bregenz
Study of the Quality of Life of Patients With Fabry Disease Aged 65 and Over With and Without Specific Treatment
N/AFabry disease is a rare genetic disorder affecting 1 in 10,000 individuals,...
Location
Groupe Hospitalier Diaconesses Croix Saint-Simon
Alternative Dosing and Regimen of Replagal to Treat Fabry Disease
PHASE2The main goal of this study is to assess the pharmacodynamic effects of dif...
Location
National Institute of Neurological Disorders and Stroke (NINDS)
Safety Study of Replagal® Therapy in Children With Fabry Disease
PHASE2The purpose of this study is to assess the safety of Replagal in children w...
Location
Emory Division of Medical Genetics